Transfection
Mucopolysaccharidosis
Genetic enhancement
HEK 293 cells
Enzyme replacement therapy
Vector (molecular biology)
Keratan sulfate
Viral vector
Lysosomal storage disease
Virology
Enzyme
Biology
Molecular biology
Medicine
Glycosaminoglycan
Recombinant DNA
Disease
Chondroitin sulfate
Gene
Internal medicine
Biochemistry